Gene Therapy


19 Feeds
  • Adeno-associated virus (AAV)-based gene therapy is a biological vector that is being researched to be used as a potential therapeutic option. This gene therapy is designed to insert fragments of DNA into targeted cells to help treat diseases, such as hemophilia a. Discover the latest research on AAV-based gene therapy here.
    AAV-based Gene Therapy

    Adeno-associated virus (AAV)-based gene therapy is a biological vector that is being researched to be used as a potential therapeutic option. This gene therapy is designed to insert fragments of DNA into targeted cells to help treat diseases, such as hemophilia a. Discover the latest research on AAV-based gene therapy here.

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  • This feed focuses on antisense oligonucleotide therapies such as Inotersen, Nusinursen, and Patisiran, in neurodegenerative diseases including amyotrophic lateral sclerosis.
    Antisense Oligonucleotide - Therapies For ALS
    Going Viral

    This feed focuses on antisense oligonucleotide therapies such as Inotersen, Nusinursen, and Patisiran, in neurodegenerative diseases including amyotrophic lateral sclerosis.

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  • This feed focuses on antisense oligonucleotide therapies such as Inotersen, Nusinursen, and Patisiran, in neurodegenerative diseases including amyotrophic lateral sclerosis.
    Antisense Oligonucleotides: ND

    This feed focuses on antisense oligonucleotide therapies such as Inotersen, Nusinursen, and Patisiran, in neurodegenerative diseases including amyotrophic lateral sclerosis.

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  • Over 1700 different mutations in the CFTR genes have been shown to cause cystic fibrosis. Here is the latest research on structural therapy for CFTR mutants.
    CFTR Mutant Structural Therapy

    Over 1700 different mutations in the CFTR genes have been shown to cause cystic fibrosis. Here is the latest research on structural therapy for CFTR mutants.

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  • Gene and cell therapy advances have shown promising outcomes for several diseases. The role of cis-regulatory elements (CREs) is crucial in the design of gene therapy vectors. Here is the latest research on CREs in gene and cell therapy.
    CREs: Gene & Cell Therapy

    Gene and cell therapy advances have shown promising outcomes for several diseases. The role of cis-regulatory elements (CREs) is crucial in the design of gene therapy vectors. Here is the latest research on CREs in gene and cell therapy.

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  • CRISPR-Cas system enables the editing of genes to create or correct mutations. This feed focuses on the application of this system for gene editing and therapy in human diseases.
    CRISPR Genome Editing & Therapy
    Fast Growing

    CRISPR-Cas system enables the editing of genes to create or correct mutations. This feed focuses on the application of this system for gene editing and therapy in human diseases.

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  • Gene therapy is a powerful tool that can potentially be used for treating neurodegenerative diseases such as amyotrophic lateral sclerosis, spinal muscular atrophy, Parkinson's disease and Alzheimer's disease. Here is the latest research.
    Gene Therapies for Neurodegenerative Diseases

    Gene therapy is a powerful tool that can potentially be used for treating neurodegenerative diseases such as amyotrophic lateral sclerosis, spinal muscular atrophy, Parkinson's disease and Alzheimer's disease. Here is the latest research.

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  • The use of DNA as a technique for treating disease is a key feature of gene therapy. This type of treatment is being investigated to either replacement of a mutated gene with a healthy copy, silence a mutated gene that is dysfunctional or insert a novel gene to help fight disease. Discover the latest research on gene therapy here.
    Gene Therapy
    Going Viral

    The use of DNA as a technique for treating disease is a key feature of gene therapy. This type of treatment is being investigated to either replacement of a mutated gene with a healthy copy, silence a mutated gene that is dysfunctional or insert a novel gene to help fight disease. Discover the latest research on gene therapy here.

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  • Gene therapy is emerging as a potential strategy for the treatment of cardiovascular diseases, such as peripheral arterial disease, ischemic heart disease, restenosis after angioplasty, vascular bypass graft occlusion and transplant-associated coronary artery disease. Discover the latest research on gene therapy for cardiovascular diseases here.
    Gene Therapy for Cardiovascular Diseases
    Influential

    Gene therapy is emerging as a potential strategy for the treatment of cardiovascular diseases, such as peripheral arterial disease, ischemic heart disease, restenosis after angioplasty, vascular bypass graft occlusion and transplant-associated coronary artery disease. Discover the latest research on gene therapy for cardiovascular diseases here.

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  • Gene therapy uses genes to treat or prevent diseases such as muscle diseases. Here are the latest discoveries pertaining to gene therapy and muscle diseases.
    Gene Therapy of Muscle Diseases
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    Gene therapy uses genes to treat or prevent diseases such as muscle diseases. Here are the latest discoveries pertaining to gene therapy and muscle diseases.

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  • Genetic engineering is a process that alters the genetic structure of an organism by removing or introducing DNA. This technique is being tested to program cells. Discover the latest research on genetic engineering to program cells here.
    Genetic Engineering to Program Cells
    Fast Growing

    Genetic engineering is a process that alters the genetic structure of an organism by removing or introducing DNA. This technique is being tested to program cells. Discover the latest research on genetic engineering to program cells here.

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  • This feed focuses on the high throughput technologies used to dissect the genetics of behavior and their associated disorders. Discover the latest research here.
    Genetics of Behaviour
    Fast Growing

    This feed focuses on the high throughput technologies used to dissect the genetics of behavior and their associated disorders. Discover the latest research here.

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  • Genome editing technologies enable the editing of genes to create or correct mutations or express genes of interest. Here is the latest research on genome editing in T- cells and their application in human diseases such as adoptive T-cell immunotherapy for cancer.
    Genome Editing & T-Cells

    Genome editing technologies enable the editing of genes to create or correct mutations or express genes of interest. Here is the latest research on genome editing in T- cells and their application in human diseases such as adoptive T-cell immunotherapy for cancer.

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  • Recent developments in genomics and further development of advanced post-genomic technologies, it will be possible to apply a more holistic analysis to genomic analysis. Discover the latest research in Genomic Techniques.
    Genomic Techniques

    Recent developments in genomics and further development of advanced post-genomic technologies, it will be possible to apply a more holistic analysis to genomic analysis. Discover the latest research in Genomic Techniques.

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  • This feed focuses on emerging cell and gene therapies, such as HIV vaccines, for treating patients living with HIV/AIDS. Discover the latest research here.
    HIV: Cell & Gene Therapy
    Fast Growing

    This feed focuses on emerging cell and gene therapies, such as HIV vaccines, for treating patients living with HIV/AIDS. Discover the latest research here.

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  • Mixed lineage leukemia-1 (MLL-1) is a particular type of acute leukemia from the mutation of the MLL/KMT2A gene. This mutation can be seen in pediatrics, adults and therapy-induced acute leukemia’s. Discover the latest research on MLL-r leukemia here.
    MLL-r Leukemia

    Mixed lineage leukemia-1 (MLL-1) is a particular type of acute leukemia from the mutation of the MLL/KMT2A gene. This mutation can be seen in pediatrics, adults and therapy-induced acute leukemia’s. Discover the latest research on MLL-r leukemia here.

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  • Gene therapy and protein engineering strategies, guided by biological principles, are allowing ligands and receptors to be developed as next-generation therapeutics with improved safety and efficacy. Discover the latest research here.
    Next-Generation Therapeutics

    Gene therapy and protein engineering strategies, guided by biological principles, are allowing ligands and receptors to be developed as next-generation therapeutics with improved safety and efficacy. Discover the latest research here.

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  • Transcription activator-like effectors (TALEs) and TALE nucleases (TALENs) enable gene editing by targeting specific DNA sequences in the genome. Here is the latest research.
    TALEs and TALENs
    Fast Growing

    Transcription activator-like effectors (TALEs) and TALE nucleases (TALENs) enable gene editing by targeting specific DNA sequences in the genome. Here is the latest research.

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  • The delivery of genes into DNA for gene therapy is done through the use of vectors, which are often viral vectors. These vectors can be manipulated to include DNA and RNA depending on the type of therapy that is needed. Here is the latest research on vector gene therapy.
    Vectors in Gene Therapy

    The delivery of genes into DNA for gene therapy is done through the use of vectors, which are often viral vectors. These vectors can be manipulated to include DNA and RNA depending on the type of therapy that is needed. Here is the latest research on vector gene therapy.

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