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AAV-based Gene Therapy

AAV-based Gene Therapy diagram by Public Domain, Wikimedia
Public Domain, Wikimedia

Adeno-associated virus (AAV)-based gene therapy is a biological vector that is being researched to be used as a potential therapeutic option. This gene therapy is designed to insert fragments of DNA into targeted cells to help treat diseases, such as hemophilia a. Discover the latest research on AAV-based gene therapy here.

Top 20 most recent papers
Molecular Therapy : the Journal of the American Society of Gene Therapy

AAV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo

Molecular Therapy : the Journal of the American Society of Gene TherapyMarch 28, 2020
Sara K PowellThomas J McCown
6
Hearing Research

Viral vectors for gene delivery to the inner ear

Hearing ResearchMarch 23, 2020
Casey A Maguire, David P Corey
Movement Disorders : Official Journal of the Movement Disorder Society

Aromatic L-Amino Acid Decarboxylase Gene Therapy Enhances Levodopa Response in Parkinson's Disease

Movement Disorders : Official Journal of the Movement Disorder SocietyMarch 10, 2020
John G NuttChadwick W Christine
12
1
Frontiers in Synaptic Neuroscience

Monosynaptic Tracing Success Depends Critically on Helper Virus Concentrations

Frontiers in Synaptic NeuroscienceMarch 3, 2020
Thomas K LavinIan R Wickersham
BMJ Open Diabetes Research & Care

Placental growth factor in beta cells plays an essential role in gestational beta-cell growth

BMJ Open Diabetes Research & CareMarch 8, 2020
Weixia YangXiangwei Xiao
1
BMC Infectious Diseases

Pre-treatment with IL2 gene therapy alleviates Staphylococcus aureus arthritis in mice

BMC Infectious DiseasesMarch 1, 2020
Berglind BergmannInger Gjertsson
1
Current Opinion in Ophthalmology

Gene therapy beyond luxturna: a new horizon of the treatment for inherited retinal disease

Current Opinion in OphthalmologyMarch 17, 2020
Dominic A PradoRamiro S Maldonado
1

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