Gene Therapies for Neurodegenerative Diseases

Gene therapy is a powerful tool that can potentially be used for treating neurodegenerative diseases such as amyotrophic lateral sclerosis, spinal muscular atrophy, Parkinson's disease and Alzheimer's disease. Here is the latest research.

September 8, 2020
Open Access

Neuronal intranuclear inclusion disease (NIID)

Rinshō shinkeigaku = Clinical neurology
Jun Sone
September 19, 2020
Review
Open Access

Novel therapies for mucopolysaccharidosis type III

Journal of Inherited Metabolic Disease
Berna Seker YilmazJulien Baruteau
September 12, 2020
Review

Direct convective delivery of adeno-associated virus gene therapy for treatment of neurological disorders

Journal of Neurosurgery
Russell R LonserKrystof S Bankiewicz
July 9, 2020
Review

Modern approaches in gene therapy of motor neuron diseases

Medicinal Research Reviews
Maria Zakharova
August 14, 2020
Review
Open Access

Recent developments in the treatment of Parkinson's Disease

F1000Research
Thomas B Stoker, Roger A Barker
September 18, 2020

Topical Ocular Delivery of Nanocarriers: A Feasible Choice for Glaucoma Management

Current Pharmaceutical Design
Karthikeyan KesavanVal C Sheffield
August 14, 2020

Age-related macular degeneration: a review of current therapies and new treatments

Arquivos brasileiros de oftalmologia
Vinicius KniggendorfCaio V Regatieri
July 9, 2020
Open Access

A Mixed-Surface Polyamidoamine Dendrimer for In Vitro and In Vivo Delivery of Large Plasmids

Pharmaceutics
Bhairavi SrinageshwarJulien Rossignol
September 11, 2020

Emerging Therapies in Friedreich's Ataxia

Expert Review of Neurotherapeutics
Theresa A ZesiewiczJoshua Vega
August 11, 2020
Review
Open Access

Effects of RAGE inhibition on the progression of the disease in hSOD1G93A ALS mice

Pharmacology Research & Perspectives
Liping LiuMariana Pehar
June 28, 2020

Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice

Molecular Therapy : the Journal of the American Society of Gene Therapy
Hannah G LaheyMiguel Sena-Esteves
August 28, 2020
Open Access

Adeno-Associated Virus-Induced Dorsal Root Ganglion Pathology

Human Gene Therapy
Juliette HordeauxJames M Wilson
September 24, 2020
Review
Open Access

Gene therapy for neurodegenerative disorders: advances, insights and prospects

Acta Pharmaceutica Sinica. B
Wei ChenDianwen Ju
August 7, 2020
Open Access

PSCs Reveal PUFA-Provoked Mitochondrial Stress as a Central Node Potentiating RPE Degeneration in Bietti's Crystalline Dystrophy

Molecular Therapy : the Journal of the American Society of Gene Therapy
Zhao ZhangQizhou Lian

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