Vectors in Gene Therapy

The delivery of genes into DNA for gene therapy is done through the use of vectors, which are often viral vectors. These vectors can be manipulated to include DNA and RNA depending on the type of therapy that is needed. Here is the latest research on vector gene therapy.

June 18, 2020
Open Access

Arginine-Modified Polymers Facilitate Poly (Lactide-Co-Glycolide)-Based Nanoparticle Gene Delivery to Primary Human Astrocytes

International Journal of Nanomedicine
Jessica ProulxKathleen Borgmann
June 17, 2020
Review
Open Access

WFH State-of-the-art paper 2020: In vivo lentiviral vector gene therapy for haemophilia

Haemophilia : the Official Journal of the World Federation of Hemophilia
Alessio Cantore, Luigi Naldini
June 21, 2020
Open Access

Development of adaptive resistance to electric pulsed field treatment in CHO cell line in vitro

Scientific Reports
Tamara Polajžer, Damijan Miklavčič
July 6, 2020
Comment / Editorial

Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions

The Journal of Allergy and Clinical Immunology
Francesca FerruaMaria Grazia Roncarolo
June 10, 2020

Mesenchymal Stem Cells: A New Generation of Therapeutic Agent Vehicles in Gene Therapy

Current Gene Therapy
Mahmoud GharbaviSaeed Ghanbarzadeh
June 12, 2020

Rescue of Advanced Pompe Disease in Mice with Hepatic Expression of Secretable Acid α-Glucosidase

Molecular Therapy : the Journal of the American Society of Gene Therapy
Umut CaginFederico Mingozzi
June 27, 2020

In vivo delivery of MMP3-shRNA and Sox9 lentivirus cocktail enhances matrix synthesis to prevent lumbar disc degeneration

Advances in Clinical and Experimental Medicine : Official Organ Wroclaw Medical University
Zheng ZhaoYongming Xi
July 6, 2020

Non-viral Gene Delivery of HIF-1α Promotes Angiogenesis in Human Adipose-Derived Stem Cells

Acta Biomaterialia
Savannah E Est-WitteJordan J Green
June 28, 2020

Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice

Molecular Therapy : the Journal of the American Society of Gene Therapy
Hannah G LaheyMiguel Sena-Esteves
June 20, 2020

Low molecular weight polyethyleneimine conjugated guar gum for targeted gene delivery to triple negative breast cancer

International Journal of Biological Macromolecules
Piyali JanaKishor Sarkar
June 25, 2020

Engineered Capsids for Efficient Gene Delivery to the Retina and Cornea

Human Gene Therapy
Amy FrederickCatherine R O'Riordan

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