A natural choice for hemophilia B.

Blood
Dwight D Koeberl

Abstract

In this issue of Blood, Crudele et al describe a novel study of adeno-associated virus (AAV) vector-mediated gene therapy that induced immune tolerance to factor IX (FIX) in a hemophilia B (HB) dog with previously formed anti-FIX inhibitor antibodies (IAs).

References

Oct 23, 2009·The New England Journal of Medicine·Paolo SimioniValder R Arruda
Dec 14, 2011·The New England Journal of Medicine·Amit C NathwaniAndrew M Davidoff
Aug 29, 2012·British Journal of Haematology·Donna M DiMichele
Oct 10, 2013·EMBO Molecular Medicine·David M MarkusicRoland W Herzog

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