Citations
Jan 8, 2019·American Journal of Medical Genetics. Part C, Seminars in Medical Genetics·Ni-Chung LeeWuh-Liang Hwu
Mar 29, 2019·Movement Disorders : Official Journal of the Movement Disorder Society·Shekeeb S MohammadRussell C Dale
Mar 14, 2019·Annals of Neurology·Chih-Hsien TsengWuh-Liang Hwu
Dec 19, 2018·The Journal of Clinical Endocrinology and Metabolism·Yasuhiro Naiki, Maki Fukami
Jun 22, 2019·Journal of Inherited Metabolic Disease·Peter Theodore Clayton
Feb 12, 2020·Human Gene Therapy·Megumi Kanao-KandaShuanglin Hao
Jul 10, 2019·Scientific Reports·Yutaka HoshinoHideyuki Okano
Dec 19, 2019·Journal of Inherited Metabolic Disease·Heiko BrennenstuhlThomas Opladen
Feb 20, 2020·Movement Disorders Clinical Practice·Serena GalosiVincenzo Leuzzi
May 6, 2020·Journal of Inherited Metabolic Disease·Toni S PearsonLisa Flint
Jan 29, 2019·Brain : a Journal of Neurology·Karin KojimaTakanori Yamagata
Feb 12, 2020·Nature Reviews. Genetics·Chengwen Li, R Jude Samulski
May 16, 2020·Journal of Human Genetics·Yongxin WenXinhua Bao
Jun 20, 2019·Operative Neurosurgery·Chun-Hwei TaiSheng-Hong Tseng
Jan 11, 2020·BMC Neurology·Berrin Monteleone, Keith Hyland
Jun 7, 2020·Journal of Neurology, Neurosurgery, and Psychiatry·Didu KariyawasamMichelle Anne Farrar
Nov 1, 2020·Neurotherapeutics : the Journal of the American Society for Experimental NeuroTherapeutics·Philip C Buttery, Roger A Barker
Nov 11, 2020·Human Gene Therapy·Françoise PiguetNathalie Cartier
Nov 17, 2020·Advanced Healthcare Materials·Yi WangDavid R Nisbet
Dec 15, 2020·Molecular Therapy : the Journal of the American Society of Gene Therapy·Jerry R MendellJacques P Tremblay
Jan 25, 2021·Advanced Drug Delivery Reviews·Ekram Ahmed ChowdhuryDhaval K Shah
Jan 23, 2021·Italian Journal of Pediatrics·Carlo FuscoCarlotta Spagnoli
Nov 12, 2020·Frontiers in Genetics·Silvia Murillo-CuestaIsabel Varela-Nieto
Feb 18, 2021·Journal of Molecular Medicine : Official Organ of the Gesellschaft Deutscher Naturforscher Und Ärzte·Xiangjun HeBo Feng
Jan 19, 2020·Archives of Biochemistry and Biophysics·Riccardo MontioliMariarita Bertoldi
May 31, 2020·The Journal of Pediatrics·Amy G FeldmanCara L Mack
Mar 26, 2021·Molecular Genetics and Metabolism Reports·Francyne KubaskiRoberto Giugliani
Mar 22, 2021·Molecular Genetics and Metabolism·Alberto BurlinaAlessandro P Burlina
Apr 10, 2021·Developmental Medicine and Child Neurology·Riccardo PrivolizziJoanne Ng
Apr 18, 2021·Trends in Pharmacological Sciences·Cole W PetersKillian S Hanlon
Apr 24, 2021·Frontiers in Neurology·Aristide MerolaKrystof Bankiewicz
May 21, 2021·Science Translational Medicine·Joanne NgManju A Kurian
May 28, 2021·Current Medical Research and Opinion·Kate WilliamsSarah Acaster
May 18, 2021·Journal of Pediatric Genetics·Vykuntaraju K GowdaSanjay K Shivappa
May 18, 2021·Molecular Genetics and Metabolism Reports·Tessa WassenbergMarcel M Verbeek
Jul 14, 2021·Nature Communications·Toni S PearsonKrystof S Bankiewicz
Jul 15, 2021·Current Medical Research and Opinion·Hanna SkrobanskiSarah Acaster
Mar 19, 2021·Brain : a Journal of Neurology·Giada RossignoliManju A Kurian
Aug 24, 2021·EMBO Molecular Medicine·Paul Wuh-Liang HwuShin-Ichi Muramatsu
Oct 15, 2021·Neurotherapeutics : the Journal of the American Society for Experimental NeuroTherapeutics·Gemma L CarvillScott Demarest
Nov 12, 2021·Molecular Therapy : the Journal of the American Society of Gene Therapy·Chun-Hwei TaiWuh-Liang Hwu
Sep 24, 2021·Current Gene Therapy·Wuh-Liang HwuBruria Gidoni-Ben-Zeev
Dec 14, 2021·The Journal of Gene Medicine·Keiji OguroShin-Ichi Muramatsu