References
Dec 5, 1998·American Journal of Hematology·J M SoucieD Jackson
Feb 23, 1999·British Journal of Haematology·D V GnatenkoW F Bahou
Jun 9, 2001·The New England Journal of Medicine·P M Mannucci, E G Tuddenham
Jan 8, 2003·Blood·Catherine S MannoBertil Glader
Feb 14, 2006·Nature Medicine·Catherine S MannoMark A Kay
Aug 21, 2007·Haemophilia : the Official Journal of the World Federation of Hemophilia·D M DiMicheleE Santagostino
Sep 22, 2007·Haemophilia : the Official Journal of the World Federation of Hemophilia·M Manco-Johnson
Aug 10, 2007·The New England Journal of Medicine·Marilyn J Manco-JohnsonBruce L Evatt
May 2, 2008·Thrombosis and Haemostasis·Steven W Pipe
Jun 29, 2011·British Journal of Haematology·Mark W Skinner
Dec 14, 2011·The New England Journal of Medicine·Amit C NathwaniAndrew M Davidoff
Jan 1, 2010·Journal of Blood Medicine·Antonio CoppolaAnna Maria Cerbone
May 29, 2012·Journal of Thrombosis and Haemostasis : JTH·E L KuetherQ Shi
Jun 22, 2012·Gene Therapy·D GaudetS van Deventer
Jul 11, 2012·Haemophilia : the Official Journal of the World Federation of Hemophilia·A SrivastavaUNKNOWN Treatment Guidelines Working Group on Behalf of The World Federation Of Hemophilia
Sep 22, 2012·Gene Therapy·J M JohnstonH T Spencer
Jan 3, 2013·Molecular Therapy : the Journal of the American Society of Gene Therapy·Mark W Skinner
Jan 18, 2013·Blood·Ashley T MartinoRoland W Herzog
Feb 28, 2013·Human Gene Therapy Methods·Vedell Louis JeuneThomas Weber
Apr 13, 2013·Journal of Hepatology·Stefano FagiuoliGiuseppe Remuzzi
Apr 19, 2013·Blood·Federico Mingozzi, Katherine A High
Nov 21, 2013·Nature Communications·Lily M DuDavid A Wilcox
Jun 14, 2014·Proceedings of the National Academy of Sciences of the United States of America·Chul-Yong ParkDong-Wook Kim
Sep 5, 2014·Biotechnology Journal·Elena SenísDirk Grimm
Nov 20, 2014·The New England Journal of Medicine·Amit C NathwaniAndrew M Davidoff
Nov 25, 2014·Human Gene Therapy·Paul Edward MonahanR Jude Samulski
Jan 2, 2015·Frontiers in Bioscience (Landmark Edition)·Geoffrey L Rogers, Roland W Herzog
Jan 6, 2015·Molecular Therapy. Methods & Clinical Development·Brandon K SackDavid M Markusic
Jan 9, 2015·Thrombosis and Haemostasis·Kathelijn FischerUNKNOWN EUHASS participants
Feb 7, 2015·Molecular Therapy : the Journal of the American Society of Gene Therapy·Xuefeng WangCarol H Miao
Feb 11, 2015·Journal of Medical Economics·Zheng-Yi ZhouMichael B Nichol
Feb 26, 2015·Blood·Johannes Oldenburg
Mar 31, 2015·British Journal of Haematology·Rolf Ljung, Nadine Gretenkort Andersson
Jul 8, 2015·Journal of Thrombosis and Haemostasis : JTH·P E Monahan
Aug 25, 2015·Blood·Rajiv SharmaKatherine A High
Sep 1, 2015·Haemophilia : the Official Journal of the World Federation of Hemophilia·M CarcaoB Ewenstein
Sep 13, 2015·Oncotarget·Sergiu ChiraIoana Berindan-Neagoe
Sep 22, 2015·Haemophilia : the Official Journal of the World Federation of Hemophilia·A O OladapoL A Valentino
Oct 28, 2015·BMC Health Services Research·Patrícia RochaFernando Araújo
Nov 3, 2015·Expert Opinion on Biological Therapy·Mark A BrimbleAndrew M Davidoff
Dec 8, 2015·Hematology·Paul E Monahan
Dec 24, 2015·Genome Biology·Matthew H Porteus
Feb 24, 2016·Expert Opinion on Orphan Drugs·Valder R Arruda, Ben J Samelson-Jones
Mar 18, 2016·Blood·Marshall A MazepaUNKNOWN US Hemophilia Treatment Center Network
Jun 4, 2016·Molecular Therapy. Methods & Clinical Development·Sandeep Rp KumarRoland W Herzog
Aug 17, 2016·Thrombosis and Haemostasis·Christopher E WalshSalvador Grancha
Aug 27, 2016·American Journal of Hematology·Jan Hartmann, Stacy E Croteau
Dec 4, 2016·Hematology·Steven W Pipe
Aug 30, 2017·Human Gene Therapy·Francesca Ferrua, Alessandro Aiuti
Citations
Sep 27, 2018·Pediatric Blood & Cancer·Courtney D Thornburg
Oct 4, 2018·Expert Review of Hematology·Guy YoungSteven Pipe
Dec 6, 2018·FASEB Journal : Official Publication of the Federation of American Societies for Experimental Biology·Jerry K Y ChanCitra N Z Mattar
Jun 23, 2019·Human Molecular Genetics·Ryotaro OmichiRichard J H Smith
Oct 15, 2019·Journal of Thrombosis and Haemostasis : JTH·Bryn M SmithCarol H Miao
Oct 14, 2019·European Journal of Haematology·Richard A MarlarDorothy M Adcock
Jun 4, 2020·Blood Advances·Beth Boulden WarrenMarilyn J Manco-Johnson
Mar 14, 2019·Blood Advances·Simone MerlinAntonia Follenzi
Jun 8, 2018·Haemophilia : the Official Journal of the World Federation of Hemophilia·S W Pipe
May 30, 2020·Haemophilia : the Official Journal of the World Federation of Hemophilia·Annette E BowyerStefan Tiefenbacher
May 16, 2020·Frontiers in Immunology·Alex C ChenCarol H Miao
Jun 18, 2020·Research and Practice in Thrombosis and Haemostasis·Flora PeyvandiThierry VandenDriessche
Sep 6, 2018·Therapeutic Advances in Hematology·Fadi Nossair, Courtney D Thornburg
Jun 6, 2019·JBJS Case Connector·Barbara MinkowitzJohn J Gregory
Dec 18, 2020·Journal of Thrombosis and Haemostasis : JTH·Steven W PipeCharles R M Hay
Oct 26, 2020·Gene·Sulaiman M Alnasser
May 30, 2020·Haematologica·Rosella FamàAntonia Follenzi
Jun 3, 2021·Biomolecules·Agnieszka Fus-KujawaAleksander L Sieron