Imperatives for DUCHENNE MD: a Simplified Guide to Comprehensive Care for Duchenne Muscular Dystrophy

PLoS Currents
Kathi KinnettKate Bushby

Abstract

Duchenne muscular dystrophy (DMD) is a progressive, life-limiting muscle-wasting disease. Although no curative treatment is yet available, comprehensive multidisciplinary care has increased life expectancy significantly in recent decades. An international consensus care publication in 2010 outlined best-practice care, which includes corticosteroid treatment, respiratory, cardiac, orthopedic and rehabilitative interventions to address disease manifestations. While disease specialists are largely aware of these care standards, local physicians responsible for the day-to-day care of patients and families may be less familiar. To facilitate optimal care, a one-page document has been generated from published care recommendations, summarizing the key elements of comprehensive care for people living with DMD ("Imperatives for Duchenne muscular dystrophy). This document was developed through an international collaboration between Parent Project Muscular Dystrophy (PPMD), United Parent Projects Muscular Dystrophy (UPPMD) and TREAT-NMD.

Citations

Oct 4, 2017·Neurology·Ronald G VictorUNKNOWN Tadalafil DMD Study Group
Feb 15, 2019·PloS One·Matthew F JacquesChristopher I Morse
Apr 28, 2017·Orphanet Journal of Rare Diseases·S RyderJ Kleijnen
May 31, 2017·The Journal of the American Osteopathic Association·Christopher Carls, Predrag Krajacic

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Software Mentioned

UPPMD
NMD
TREAT

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