References
Jan 22, 2004·Neuromuscular Disorders : NMD·Eugenio MercuriChristina Brahe
Oct 6, 2005·Neuromuscular Disorders : NMD·E BertiniK Zerres
Jan 24, 2006·Neuromuscular Disorders : NMD·E MercuriE Bertini
Jun 6, 2006·Neuromuscular Disorders : NMD·Kristin J KrosschellKathryn J Swoboda
Nov 4, 2006·Neurology·E MercuriC Brahe
Jul 31, 2007·Neuromuscular Disorders : NMD·Jessica M O'HagenDarryl C De Vivo
Jun 27, 2008·Neuromuscular Disorders : NMD·Marika PaneEugenio Mercuri
Jul 4, 2008·Neuromuscular Disorders : NMD·Carole BérardChristine Payan
May 15, 2009·PloS One·Kathryn J SwobodaLouise R Simard
Mar 10, 2010·Neurology·J MontesUNKNOWN Muscle Study Group and the Pediatric Neuromuscular Clinical Research Network
Jul 9, 2010·Neuromuscular Disorders : NMD·Douglas M SproulePetra Kaufmann
Sep 3, 2010·PloS One·Kathryn J SwobodaUNKNOWN Project Cure Spinal Muscular Atrophy Investigators Network
Sep 22, 2010·Neurology·Wendy KingRichard S Finkel
Jun 24, 2011·Muscle & Nerve·Kristin J KrosschellUNKNOWN Project Cure SMA
Apr 21, 2012·Lancet Neurology·Eugenio MercuriSusan T Iannaccone
Oct 19, 2012·Neurology·Petra KaufmannUNKNOWN Pediatric Neuromuscular Clinical Research Network for Spinal Muscular Atrophy (PNCR)
Feb 6, 2013·Archives of Physical Medicine and Rehabilitation·Carole VuillerotUNKNOWN MFM Spinal Muscular Atrophy Study Group
Mar 22, 2013·Orphanet Journal of Rare Diseases·Nathalie KayadjanianKevin Talbot
Jul 3, 2013·Neuromuscular Disorders : NMD·E MazzoneE Mercuri
Feb 5, 2014·Neuromuscular Disorders : NMD·E MazzoneE Mercuri
Oct 14, 2014·Neuromuscular Disorders : NMD·Stephen LynnVolker Straub
Citations
Nov 8, 2016·PloS One·A LoMauroG Baranello
Dec 28, 2016·Annals of Neurology·Michelle A FarrarMatthew C Kiernan
Feb 22, 2017·PloS One·Danielle RamseyFrancesco Muntoni
Jun 24, 2017·Gene Therapy·K Talbot, E F Tizzano
Jun 21, 2018·Pediatric Physical Therapy : the Official Publication of the Section on Pediatrics of the American Physical Therapy Association·Rachel SalazarDarryl C De Vivo
Jul 17, 2018·The Annals of Pharmacotherapy·Melanie K ClabornBrooke L Gildon
Jul 27, 2018·PloS One·Aurélie ChabanonUNKNOWN NatHis-SMA study group
Dec 2, 2017·European Journal of Neurology : the Official Journal of the European Federation of Neurological Societies·R I WadmanW L van der Pol
Feb 5, 2019·PharmacoEconomics·Santiago Zuluaga-SanchezAndrew Lloyd
Jan 25, 2019·Muscle & Nerve·Maria Carmela PeraUNKNOWN iSMAC Consortium Group
May 6, 2019·European Journal of Human Genetics : EJHG·Clara Serra-Juhe, Eduardo F Tizzano
Dec 30, 2018·Journal of Medical Genetics·Francesco Danilo TizianoLucia Morandi
Jul 13, 2019·Muscle & Nerve·Jacqueline MontesUNKNOWN CS2 and CS12 Study Groups
Sep 3, 2019·Journal of Neuromuscular Diseases·A M B van der HeulL van den Engel-Hoek
Aug 28, 2019·Neurology·Eugenio MercuriMarika Pane
Apr 26, 2019·Neurology·Emma Ciafaloni, Barry S Russman
Apr 26, 2019·Neurology·Basil T DarrasUNKNOWN ISIS-396443-CS2/ISIS-396443-CS12 Study Groups
Jan 30, 2020·Biomedicines·Silvia BonannoLorenzo Maggi
Feb 15, 2018·The New England Journal of Medicine·Eugenio MercuriUNKNOWN CHERISH Study Group
Jul 19, 2020·NMR in Biomedicine·Louise A M OttoMartijn Froeling
Feb 1, 2020·Annual Review of Genomics and Human Genetics·Brunhilde WirthNatalia Mendoza-Ferreira
Sep 13, 2020·Journal of Neurology, Neurosurgery, and Psychiatry·Lorenzo MaggiElena Pegoraro
Aug 12, 2020·European Journal of Neurology : the Official Journal of the European Federation of Neurological Societies·B StolteT Hagenacker
Oct 2, 2020·Continuum : Lifelong Learning in Neurology·Jessica Rose Nance
Aug 20, 2017·Orphanet Journal of Rare Diseases·Julio López-BastidaJuan Oliva-Moreno
Jul 7, 2018·Child Neurology Open·Christina StarkEckhard Schoenau
Oct 3, 2018·Frontiers in Neurology·Antonella LoMauroAndrea Aliverti
Dec 20, 2018·Journal of Neuromuscular Diseases·Sally Dunaway YoungDarryl C De Vivo
Jun 5, 2020·The Canadian Journal of Neurological Sciences. Le Journal Canadien Des Sciences Neurologiques·Victoria L HodgkinsonLawrence Korngut
Apr 26, 2020·Journal of Neuromuscular Diseases·Crystal Jing Jing YeoKathryn J Swoboda
May 4, 2020·Journal of Neurology·Alma OsmanovicOlivia Schreiber-Katz
Feb 25, 2017·BMC Neurology·Maria C PeraEugenio Mercuri
May 12, 2017·Annals of Clinical and Translational Neurology·Ulrike BonatiChristian Czech
Oct 7, 2017·Current Neurology and Neuroscience Reports·Diana Bharucha-Goebel, Petra Kaufmann
Dec 26, 2018·Journal of Managed Care & Specialty Pharmacy·Vamshi K RaoMary Schroth
Oct 15, 2019·Frontiers in Genetics·Alireza ShahryariHeiko Lickert
Jun 18, 2019·Therapeutic Advances in Neurological Disorders·Claudia D WursterMarkus Otto
Mar 22, 2019·Wiley Interdisciplinary Reviews. RNA·Sara Nik, Teresa V Bowman
Mar 14, 2020·Orphanet Journal of Rare Diseases·Hamish W Y WanMichelle A Farrar
Sep 19, 2020·PloS One·Dylan TrundellCarole Vuillerot
Apr 16, 2020·Orphanet Journal of Rare Diseases·Bart BartelsW Ludo van der Pol
Oct 9, 2019·Journal of Neuromuscular Diseases·Maggie C WalterBenedikt Schoser
Aug 1, 2020·Neurology·Camiel A WijngaardeW Ludo van der Pol
Oct 20, 2020·Journal of Neuromuscular Diseases·Rodrigo H MendonçaEdmar Zanoteli
Nov 9, 2020·BMC Musculoskeletal Disorders·Agnieszka StępieńMaria Jędrzejowska
Jan 13, 2021·Medicine·Jin-Mo ParkJin-Sung Park
Jan 23, 2021·NMR in Biomedicine·Louise A M OttoW-Ludo van der Pol
Jul 1, 2020·Pediatric Physical Therapy : the Official Publication of the Section on Pediatrics of the American Physical Therapy Association·Jacqueline Montes, Lisa H Yoon
Oct 5, 2020·European Journal of Neurology : the Official Journal of the European Federation of Neurological Societies·V A SansoneUNKNOWN Italian ISMAC group
Oct 27, 2020·Journal of Neuromuscular Diseases·Lisa BelterAngela D Paradis