Update on Standard Operating Procedures in Preclinical Research for DMD and SMA Report of TREAT-NMD Alliance Workshop, Schiphol Airport, 26 April 2015, The Netherlands

Journal of Neuromuscular Diseases
Maaike van PuttenRaffaella Willmann

Abstract

A workshop took place in 2015 to follow up TREAT-NMD activities dedicated to improving quality in the preclinical phase of drug development for neuromuscular diseases. In particular, this workshop adressed necessary future steps regarding common standard experimental protocols and the issue of improving the translatability of preclinical efficacy studies.

References

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May 21, 2017·Skeletal Muscle·Joe N Kornegay

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Citations

Dec 18, 2018·Developmental Medicine and Child Neurology·Rudolf Korinthenberg
Feb 1, 2020·Expert Opinion on Drug Discovery·Nalinda B WasalaDongsheng Duan

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Methods Mentioned

BETA
SMA

Software Mentioned

TREAT
GRMD
PROM
Upper
NMD
Bio

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